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687. Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Genome Editing
Abstract   Open access   Peer reviewed

687. Therapeutic Correction of an LCA-Causing Splice Defect in the CEP290 Gene by CRISPR/Cas-Mediated Genome Editing

Morgan L Maeder, Shen Shen, Erin R Burnight, Sebastian Gloskowski, Rina Mepani, Ari E Friedland, Hari Jayaram, Greg Gotta, Budd A Tucker and David Bumcrot
Molecular therapy, Vol.23, pp.S273-S274
05/2015
DOI: 10.1016/S1525-0016(16)34296-4
url
https://doi.org/10.1016/S1525-0016(16)34296-4View
Published (Version of record) Open Access

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