- Title: Subtitle
- Fabry patient's experience of pegunigalsidase alfa monthly infusion: PEOPLE study
- Creators
- Ankit MehtaFrancois J. EyskensAntonio PisaniUlla Feldt-RasmussenDerralynn HughesPatrick B. DeeganOzlem Goker-AlpanEric WallaceJohn BernatNicola LongoFrancesco BianchiRossana RoccoYlenia Paleari
- Resource Type
- Abstract
- Publication Details
- Molecular genetics and metabolism, Vol.141(2), 107961
- DOI
- 10.1016/j.ymgme.2023.107961
- ISSN
- 1096-7192
- eISSN
- 1096-7206
- Language
- English
- Date published
- 02/2024
- Academic Unit
- Stead Family Department of Pediatrics; Medical Genetics and Genomics
- Record Identifier
- 9984557959202771
Abstract
Fabry patient's experience of pegunigalsidase alfa monthly infusion: PEOPLE study
Molecular genetics and metabolism, Vol.141(2), 107961
02/2024
DOI: 10.1016/j.ymgme.2023.107961
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