- Title: Subtitle
- Quantification of dystrophin to assess the effects of dystrophin-restoring treatments in Duchenne muscular dystrophy: Lessons from the development of eteplirsen
- Creators
- Johannes DworzakDiane E FrankJay S CharlestonFrederick J SchnellJon VossCas DonoghueAnthony J MiliciFamke AeffnerG. David YoungSteven A MooreSarah LewisEllyn PetersonZarife SahenkKimberly ShontzLouise R Rodino-KlapacJerry R Mendell
- Resource Type
- Abstract
- Publication Details
- European journal of paediatric neurology, Vol.21, pp.e93-e94
- DOI
- 10.1016/j.ejpn.2017.04.1209
- ISSN
- 1090-3798
- eISSN
- 1532-2130
- Language
- English
- Date published
- 06/2017
- Academic Unit
- Pathology
- Record Identifier
- 9984201527902771
Abstract
Quantification of dystrophin to assess the effects of dystrophin-restoring treatments in Duchenne muscular dystrophy: Lessons from the development of eteplirsen
European journal of paediatric neurology, Vol.21, pp.e93-e94
06/2017
DOI: 10.1016/j.ejpn.2017.04.1209
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