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Small molecule therapies for juvenile neuronal ceroid lipofuscinosis
Abstract   Peer reviewed

Small molecule therapies for juvenile neuronal ceroid lipofuscinosis

Rebecca C Ahrens-Nicklas, Luis Tecedor, Mark L Schultz, Elena Lysenko, Shyam Ramachandran, Eric D Marsh and Beverly L Davidson
Molecular genetics and metabolism, Vol.120(1-2), pp.S18-S19
01/2017
DOI: 10.1016/j.ymgme.2016.11.015

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