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CFTR‐Associated Pancreatic Disease
Book chapter

CFTR‐Associated Pancreatic Disease

Chee Y Ooi and Aliye Uc
The Pancreas, pp.390-395
John Wiley & Sons, Ltd, Fourth edition
08/07/2023
DOI: 10.1002/9781119876007.ch47

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Abstract

Cystic fibrosis transmembrane conductance regulator ( CFTR ) is critical for pancreas health. Its deficiency leads to a variety of pancreatic damage from recurrent inflammation to chronic damage, exocrine pancreatic insufficiency, diabetes, and potentially cancer. Emerging therapies suggest that correcting and/or modulating CFTR function in the pancreas may prevent recurrent attacks of pancreatitis in people with cystic fibrosis and potentially delay or reverse ongoing pancreatic destruction.
Cystic Fibrosis Gene Therapy acute recurrent pancreatitis CFTR correctors CFTR potentiators chronic pancreatitis diabetes mellitus exocrine pancreatic insufficiency pancreatic enzymes sweat chloride

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