Logo image
A Randomized Double-Blind Trial of Hydroxychloroquine for the Prevention of Chronic Graft-versus-Host Disease after Allogeneic Peripheral Blood Stem Cell Transplantation
Journal article   Open access   Peer reviewed

A Randomized Double-Blind Trial of Hydroxychloroquine for the Prevention of Chronic Graft-versus-Host Disease after Allogeneic Peripheral Blood Stem Cell Transplantation

Thomas Fong, Kathryn Trinkaus, Douglas Adkins, Ravi Vij, Steven M Devine, Michael Tomasson, Lawrence T Goodnough, Sandra Lopez, Timothy Graubert, Shalini Shenoy, …
Biology of blood and marrow transplantation, Vol.13(10), pp.1201-1206
2007
DOI: 10.1016/j.bbmt.2007.06.012
PMID: 17889357
url
https://doi.org/10.1016/j.bbmt.2007.06.012View
Published (Version of record) Open Access

Abstract

Hydroxychloroquine (HCQ) is an immunosuppressive lysosomotropic amine that has activity against graft-versus-host disease (GVHD). In a single-institution phase III trial, 95 recipients of allogeneic peripheral blood stem cell (PBSC) transplantation were randomized to receive, in a double-blind fashion, and in addition to prophylactic cyclosporine A (CSA), HCQ, or placebo starting 21 days pretransplant and continued until day +365. HCQ was very well tolerated and not associated with side effects. Overall, the incidence of acute GVHD (aGVHD) was 59% in both arms, and severe aGVHD occurred in 11% (HCQ) and 14% (placebo) ( P = .76). Sixty percent and 78% of patients developed chronic GVHD (cGVHD) in the HCQ and the placebo arms, respectively ( P = .15). With a median follow-up of 18 months, relapse-free and overall survivals (OS) were comparable in both groups. In summary, in this randomized trial, the addition of HCQ to single-agent CSA had no effects on aGVHD or cGVHD or survival.
Hydroxycholorquine Propyhlaxis Chronic GVHD

Details

Metrics

Logo image