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Estimating a treatment effect with repeated measurements accounting for varying effectiveness duration
Journal article   Open access   Peer reviewed

Estimating a treatment effect with repeated measurements accounting for varying effectiveness duration

Y. Q Chen, J Yang, S Cheng and J. B Jackson
Biometrika, Vol.94(2), pp.387-402
06/2007
DOI: 10.1093/biomet/asm019
url
https://doi.org/10.1093/biomet/asm019View
Published (Version of record) Open Access

Abstract

To assess treatment efficacy in clinical trials, certain clinical outcomes are repeatedly measured over time for the same subject. The difference in their means may characterize a treatment effect. Since treatment effectiveness lag and saturation times may exist, erosion of treatment effect often occurs during the observation period. Instead of using models based on ad hoc parametric or purely nonparametric time-varying coefficients, we model the treatment effectiveness durations, which are the time intervals between the lag and saturation times. Then we use some mean response models to include such treatment effectiveness durations. Our methodology is demonstrated by simulations and analysis of a landmark HIV/AIDS clinical trial of short-course nevirapine against mother-to-child HIV vertical transmission during labour and delivery.
clinical trial mean response model time-varying coefficient longitudinal study effect erosion /

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