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Pharmacological ascorbate with gemcitabine for the control of metastatic and node-positive pancreatic cancer (PACMAN): results from a phase I clinical trial
Journal article   Open access   Peer reviewed

Pharmacological ascorbate with gemcitabine for the control of metastatic and node-positive pancreatic cancer (PACMAN): results from a phase I clinical trial

J. L WELSH, B. A WAGNER, J DRISKO, M LEVINE, G. R BUETTNER, J. J CULLEN, T. J VAN'T ERVE, P. S ZEHR, D. J BERG, T. R HALFDANARSON, …
Cancer chemotherapy and pharmacology, Vol.71(3), pp.765-775
2013
DOI: 10.1007/s00280-013-2070-8
PMCID: PMC3587047
PMID: 23381814
url
https://www.ncbi.nlm.nih.gov/pmc/articles/3587047View
Open Access

Abstract

Background Treatment for pancreatic cancer with pharmacological ascorbate (ascorbic acid, vitamin C) decreases tumor progression in preclinical models. A phase I clinical trial was performed to establish safety and tolerability of pharmacological ascorbate combined with gemcitabine in patients with biopsy-proven stage IV pancreatic adenocarcinoma. Design Nine subjects received twice-weekly intravenous ascorbate (15–125 g) employing Simon’s accelerated titration design to achieve a targeted post-infusion plasma level of ≥350 mg/dL (≥20 mM). Subjects received concurrent gemcitabine. Disease burden, weight, performance status, hematologic and metabolic laboratories, time to progression and overall survival were monitored. Results Mean plasma ascorbate trough levels were significantly higher than baseline (1.46 ± 0.02 vs. 0.78 ± 0.09 mg/dL, i.e., 83 vs. 44 μM, p < 0.001). Adverse events attributable to the drug combination were rare and included diarrhea (n = 4) and dry mouth (n = 6). Dose-limiting criteria were not met for this study. Mean survival of subjects completing at least two cycles (8 weeks) of therapy was 13 ± 2 months. Conclusions Data suggest pharmacologic ascorbate administered concurrently with gemcitabine is well tolerated. Initial data from this small sampling suggest some efficacy. Further studies powered to determine efficacy should be conducted.
Antineoplastic Agents Tumors Gastroenterology. Liver. Pancreas. Abdomen Liver. Biliary tract. Portal circulation. Exocrine pancreas Pharmacology. Drug treatments Biological and medical sciences Multiple tumors. Solid tumors. Tumors in childhood (general aspects) Medical sciences

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