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Small-molecule ion channels increase host defences in cystic fibrosis airway epithelia
Journal article   Peer reviewed

Small-molecule ion channels increase host defences in cystic fibrosis airway epithelia

Katrina A Muraglia, Rajeev S Chorghade, Bo Ram Kim, Xiao Xiao Tang, Viral S Shah, Anthony S Grillo, Page N Daniels, Alexander G Cioffi, Philip H Karp, Lingyang Zhu, …
Nature (London), Vol.567(7748), pp.405-408
03/2019
DOI: 10.1038/s41586-019-1018-5
PMCID: PMC6492938
PMID: 30867598

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Abstract

Loss-of-function mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) compromise epithelial HCO and Cl secretion, reduce airway surface liquid pH, and impair respiratory host defences in people with cystic fibrosis . Here we report that apical addition of amphotericin B, a small molecule that forms unselective ion channels, restored HCO secretion and increased airway surface liquid pH in cultured airway epithelia from people with cystic fibrosis. These effects required the basolateral Na , K -ATPase, indicating that apical amphotericin B channels functionally interfaced with this driver of anion secretion. Amphotericin B also restored airway surface liquid pH, viscosity, and antibacterial activity in primary cultures of airway epithelia from people with cystic fibrosis caused by different mutations, including ones that do not yield CFTR, and increased airway surface liquid pH in CFTR-null pigs in vivo. Thus, unselective small-molecule ion channels can restore host defences in cystic fibrosis airway epithelia via a mechanism that is independent of CFTR and is therefore independent of genotype.
Amphotericin B - pharmacology Animals Bicarbonates - metabolism Cells, Cultured Cystic Fibrosis - genetics Cystic Fibrosis - metabolism Cystic Fibrosis Transmembrane Conductance Regulator - deficiency Cystic Fibrosis Transmembrane Conductance Regulator - genetics Cystic Fibrosis Transmembrane Conductance Regulator - metabolism Epithelial Cells - cytology Epithelial Cells - drug effects Epithelial Cells - metabolism Epithelium - drug effects Epithelium - metabolism Female Humans Hydrogen-Ion Concentration Ion Channels - metabolism Male Respiratory Mucosa - drug effects Respiratory Mucosa - metabolism Respiratory System - drug effects Respiratory System - metabolism Sodium-Potassium-Exchanging ATPase - metabolism Swine

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