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Targeting CBLB as a potential therapeutic approach for disseminated candidiasis
Journal article   Peer reviewed

Targeting CBLB as a potential therapeutic approach for disseminated candidiasis

Yun Xiao, Juan Tang, Hui Guo, Yixia Zhao, Rong Tang, Song Ouyang, Qiuming Zeng, Chad A Rappleye, Murugesan V S Rajaram, Larry S Schlesinger, …
Nature medicine, Vol.22(8), pp.906-914
08/2016
DOI: 10.1038/nm.4141
PMCID: PMC4975523
PMID: 27428899

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Abstract

Disseminated candidiasis has become one of the leading causes of hospital-acquired blood stream infections with high mobility and mortality. However, the molecular basis of host defense against disseminated candidiasis remains elusive, and treatment options are limited. Here we report that the E3 ubiquitin ligase CBLB directs polyubiquitination of dectin-1 and dectin-2, two key pattern-recognition receptors for sensing Candida albicans, and their downstream kinase SYK, thus inhibiting dectin-1- and dectin-2-mediated innate immune responses. CBLB deficiency or inactivation protects mice from systemic infection with a lethal dose of C. albicans, and deficiency of dectin-1, dectin-2, or both in Cblb(-/-) mice abrogates this protection. Notably, silencing the Cblb gene in vivo protects mice from lethal systemic C. albicans infection. Our data reveal that CBLB is crucial for homeostatic control of innate immune responses mediated by dectin-1 and dectin-2. Our data also indicate that CBLB represents a potential therapeutic target for protection from disseminated candidiasis.
Immunoprecipitation Candida albicans Dendritic Cells - immunology Humans Immunity, Innate - genetics Candidiasis, Invasive - genetics Phagocytosis - genetics Gene Knockdown Techniques Lectins, C-Type - metabolism Reactive Oxygen Species - immunology Leukocytes, Mononuclear - immunology Adaptor Proteins, Signal Transducing - immunology Macrophages - immunology Cytokines - immunology Proto-Oncogene Proteins c-cbl - genetics Mutagenesis, Site-Directed Enzyme-Linked Immunosorbent Assay Neutrophils - immunology Phagocytosis - immunology Ubiquitination - immunology Blotting, Western Mice, Knockout Immunity, Innate - immunology Microscopy, Confocal Syk Kinase - metabolism Animals Candidiasis, Invasive - immunology Inflammasomes - immunology Adaptor Proteins, Signal Transducing - genetics Mice Ubiquitination - genetics Proto-Oncogene Proteins c-cbl - immunology

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