CRISPR/Cas9-Edited Exa-cel Gene Therapy for Sickle Cell Disease

Letter/Communication

Anjali Sharathkumar

NEJM journal watch. Oncology & hematology

05/08/2024

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Exagamglogene autotemcel shows promise for adolescents and young adults with severe sickle cell disease.

Gene Therapy

CRISPR

Hemoglobin

Patients

Sickle cell disease

Title: Subtitle: CRISPR/Cas9-Edited Exa-cel Gene Therapy for Sickle Cell Disease
Creators: Anjali Sharathkumar
Resource Type: Letter/Communication
Publication Details: NEJM journal watch. Oncology & hematology
Publisher: Massachusetts Medical Society
ISSN: 2330-0426
Language: English
Date published: 05/08/2024
Academic Unit: Stead Family Department of Pediatrics; Hematology/Oncology
Record Identifier: 9984626998002771

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