Letter/Communication
Promise of Gene Therapy for Hemophilia A and B
NEJM journal watch. Oncology & hematology
02/24/2023
Abstract
In two single-arm phase 3 trials, gene therapy was effective in reducing bleeding at ≈2 years, but questions about long-term durability and safety remain.
Details
- Title: Subtitle
- Promise of Gene Therapy for Hemophilia A and B
- Creators
- Anjali Sharathkumar
- Resource Type
- Letter/Communication
- Publication Details
- NEJM journal watch. Oncology & hematology
- Publisher
- Massachusetts Medical Society
- ISSN
- 2330-0426
- Language
- English
- Date published
- 02/24/2023
- Academic Unit
- Stead Family Department of Pediatrics; Hematology/Oncology
- Record Identifier
- 9984375458102771
Metrics
5 Record Views