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Use of recombinant gene delivery vectors for treating or preventing lysosomal storage disorders
Patent   Open access

Use of recombinant gene delivery vectors for treating or preventing lysosomal storage disorders

Beverly Davidson, Douglas J Jolly, Sybille L Sauter, Colleen S Stein, Thomas W Dubensky Jr and Jason A Heth
United States Patent and Trademark Office
04/25/2006
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Abstract

Gene delivery vectors, such as, for example, recombinant FIV vectors, and methods of using such vectors are provided for use in treating or preventing retinal diseases of the eye and diseases of the brain associated with lysosomal storage disorders.

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