Access to novel therapies for Duchenne muscular dystrophy—Insights from expert treating physicians

Aravindhan Veerapandiyan; Anne M. Connolly; Katherine D. Mathews; Stanley Nelson; Craig McDonald; Richard S. Finkel; Vettaikorumakankav Vedanarayanan; Cuixia Tian; Susan Apkon; Julie A. Parsons; Jonathan H. Soslow; William Bryan Burnette; Kaitlin Y. Batley; Susan T. Iannaccone; Carolina Tesi Rocha; Kevin M. Flanigan; Diana Bharucha-Goebel; Sarah Wright; Migvis Monduy; Simona Treidler; Ashutosh Kumar; Nancy L. Kuntz; Vamshi K. Rao; Rachel Schrader; Saunder M. Bernes; Vikki Ann Stefans; Jena M. Krueger; Marcia V. Felker; Omer Abdul Hamid; Arpita Lakhotia; Susan Matesanz; Partha S. Ghosh; Natalie Katz; Hoda Abdel-Hamid; Chamindra G. Laverty; Bo Hoon Lee; Amy Harper; Leigh Ramos-Platt; Diana Castro; Russell J. Butterfield; Crystal M. Proud; Craig M. Zaidman; Emma Ciafaloni

doi:10.1002/cns3.20076

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Access to novel therapies for Duchenne muscular dystrophy—Insights from expert treating physicians

Journal article

Open access

Access to novel therapies for Duchenne muscular dystrophy—Insights from expert treating physicians

Aravindhan Veerapandiyan, Anne M. Connolly, Katherine D. Mathews, Stanley Nelson, Craig McDonald, Richard S. Finkel, Vettaikorumakankav Vedanarayanan, Cuixia Tian, Susan Apkon, Julie A. Parsons, …

Annals of the Child Neurology Society, Vol.2(3), pp.184-188

09/2024

DOI: 10.1002/cns3.20076

PMCID: PMC13359242

PMID: 42563918

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Title: Subtitle: Access to novel therapies for Duchenne muscular dystrophy—Insights from expert treating physicians
Creators: Aravindhan Veerapandiyan - Arkansas Children's Hospital
Anne M. Connolly - Nationwide Children's Hospital
Katherine D. Mathews - University of Iowa
Stanley Nelson - University of California, Los Angeles
Craig McDonald - University of California, Davis
Richard S. Finkel - St. Jude Children's Research Hospital
Vettaikorumakankav Vedanarayanan - The University of Texas at Austin
Cuixia Tian - University of Cincinnati
Susan Apkon - Children's Hospital Colorado
Julie A. Parsons - Children's Hospital Colorado
Jonathan H. Soslow - Vanderbilt University Medical Center
William Bryan Burnette - Vanderbilt University Medical Center
Kaitlin Y. Batley - The University of Texas Southwestern Medical Center
Susan T. Iannaccone - The University of Texas Southwestern Medical Center
Carolina Tesi Rocha - Palo Alto University
Kevin M. Flanigan - Nationwide Children's Hospital
Diana Bharucha-Goebel - Children's National
Sarah Wright - Children's National
Migvis Monduy - Miami Children's Hospital
Simona Treidler - Stony Brook University
Ashutosh Kumar - Penn State Milton S. Hershey Medical Center
Nancy L. Kuntz - Lurie Children's Hospital
Vamshi K. Rao - Northwestern University
Rachel Schrader - Parent Project Muscular Dystrophy
Saunder M. Bernes - Barrow Neurological Institute
Vikki Ann Stefans - University of Arkansas for Medical Sciences
Jena M. Krueger - Helen DeVos Children's Hospital
Marcia V. Felker - Riley Hospital for Children
Omer Abdul Hamid - Nemours Children's Clinic
Arpita Lakhotia - University of Louisville
Susan Matesanz - Children's Hospital of Philadelphia
Partha S. Ghosh - Boston Children's Hospital
Natalie Katz - Duke Medical Center
Hoda Abdel-Hamid - University of Pittsburgh
Chamindra G. Laverty - University of California San Diego
Bo Hoon Lee - University of Rochester Medicine
Amy Harper - Children's Hospital of Richmond at VCU
Leigh Ramos-Platt - University of Southern California
Diana Castro - Neurology and Neuromuscular Care Center Denton Texas USA
Russell J. Butterfield - University of Utah
Crystal M. Proud - Children's Hospital of The King's Daughters
Craig M. Zaidman - St. Louis Children's Hospital
Emma Ciafaloni - University of Rochester Medicine
Resource Type: Journal article
Publication Details: Annals of the Child Neurology Society, Vol.2(3), pp.184-188
DOI: 10.1002/cns3.20076
PMID: 42563918
PMCID: PMC13359242
NLM abbreviation: Ann Child Neurol Soc
ISSN: 2831-3267
eISSN: 2831-3267
Language: English
Electronic publication date: 06/11/2024
Date published: 09/2024
Academic Unit: Neurology; Stead Family Department of Pediatrics; Iowa Neuroscience Institute; Neurology (Pediatrics)
Record Identifier: 9984649155402771

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